Identity Tolerance Inflammation Duchenne muscular dystrophy Click chemistry Innate immunity Analytical ultracentrifugation Accelerometry GC-content GRMD dog Gait assessment Dystrophin Gene therapy High-throughput sequencing Age B-Lymphocytes/immunology/metabolism Cone photoreceptors Homologous recombination Skeletal muscle Intrathymic gene transfer DMD Genes Homopolymers Adenoassociated viral vector CNS Immunogenicity Calcium Eye surgery In vivo Vector DMDmdx rat Exercise GRMD AAV vector AAV vectors Dose study Assembly-activating protein Capsid thermostability Capsid thermal stability Acute treatment Identity assay Cell–virus interaction CMC Cell therapy Immune responses Gene transfer Baculovirus Manufacturing Inherited retinal dystrophies Duchenne Immunomodulation Clinical trial AAV Gene Therapy Immune response Dynamin 2 Humoral immunity Intra-cerebrospinal fluid injection Homogeneity Animal model High-throughput technology Gene Transfer Treg Air tamponade Immunogenicity inflammation gene therapy AAV Capsid assembly Crigler–Najjar Syndrome Congenital amaurosis Beta-subunit Centronuclear myopathy Gene-therapy ABCA4 Bioconjugates Insect cells Bioorthogonality Mice Infectivity AUC AAP Engineering Clinical trials Immunosuppression Quality control Animals Cerebellum Fluid-air exchange CD8 + T lymphocytes Adenoviridae/immunology Intravitreal Impurities Discriminant analysis Exon skipping Ectopic expression Human-monocyte-derived dendritic cells Antibody responses Capsid Antibodies/immunology/metabolism Baculovirus expression vector Childhood blindness Adeno-associated virus